Pre-malignant Clonal Evolution in Telomere Biology Disorders (TBD)

Awardee: Daria Babushok

Institution: University of Pennsylvania

Award Amount: $62,664

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Characterisation of CRB1 patient human iPSC-derived retinal organoids to set-up potency assays for gene therapy

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Do osteoclasts mediate bone marrow fibrosis in fibrous dysplasia?