Characterisation of CRB1 patient human iPSC-derived retinal organoids to set-up potency assays for gene therapy MDBRCRB1 Feb 1 Written by Million Dollar Bike Ride Awardee: Jan WijnholdsInstitution: Leiden University MedicalAward Amount: $40,177 MDBRCRB12019 Million Dollar Bike Ride Previous Previous A study of the correlation between gait abnormalities, activity monitoring parameters, CMTPeds and a biomarker in children with Charcot-Marie-Tooth disease Next Next Pre-malignant Clonal Evolution in Telomere Biology Disorders (TBD)
Characterisation of CRB1 patient human iPSC-derived retinal organoids to set-up potency assays for gene therapy MDBRCRB1 Feb 1 Written by Million Dollar Bike Ride Awardee: Jan WijnholdsInstitution: Leiden University MedicalAward Amount: $40,177 MDBRCRB12019 Million Dollar Bike Ride