Airway Cell Therapy for Cystic Fibrosis Nonsense Mutations

Awardee: Nigel Farrow

Institution: University of Adelaide, South Australia, Australia.

Award Amount: $53,668

Funding Period: February 1, 2019 - January 31, 2020

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Vitamin E Supplementation in Hyperinsulinism/Hyperammonemia Syndrome

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Zebrafish as model to analyze CDKL5 function