Epigenetic Therapy to Treat Pitt-Hopkins Syndrome (PTHS) 2017Pitt Hopkins Jan 1 Written by Million Dollar Bike Ride Awardee: Andrew KennedyInstitution: Bates CollegeAward Amount: $49,263Funding Period: January 1, 2018 - December 31, 2018 MDBR2017Pitt Hopkins Million Dollar Bike Ride Previous Previous Self-immolating NanoSpermine (nSpm) as a novel treatment approach to restore normal spermine/spermidine ratios in Snyder-Robinson Syndrome (SRS) models. Next Next AAVrh.10-mediated Npc2 Gene transfer for the treatment of Npc2 Deficient Niemann-Pick disease
Epigenetic Therapy to Treat Pitt-Hopkins Syndrome (PTHS) 2017Pitt Hopkins Jan 1 Written by Million Dollar Bike Ride Awardee: Andrew KennedyInstitution: Bates CollegeAward Amount: $49,263Funding Period: January 1, 2018 - December 31, 2018 MDBR2017Pitt Hopkins Million Dollar Bike Ride