Urokinase as a potential biomarker and target in LAM

Awardee: Victoria Stepanova

Institution: University of Pennsylvania

Award Amount: $50,000

Funding Period: January 1, 2017 - December 31, 2017

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Health related quality of life for Egyptian children with Crigler-Najjar type1

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Carboxyl lysosphingomyelin as a Biomarker for Diagnosis and Assessment of Treatment of NPC Disease