Biodistribution of Intrathecal AAV9-mediated Gene Therapy in AMN

Awardee: Florian Eichler

Institution: Massachusetts General Hospital

Award Amount: $100,000

Funding Period: January 1, 2017 - December 31, 2017

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Genomic analysis of idiopathic multicentric Castleman disease

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Understanding neurogenesis in MPS IIIA disease