Identification of Molecular Targets for Pitt-Hopkins Syndrome Treatments

Awardee: Benjamin Philpot

Institution: University of North Carolina, Chapel Hill

Award Amount: $55,000

Funding Period: January 1, 2015 - December 31, 2015

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Targeting miR-155 as a therapy for mucolipidosis IV

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Understanding TCF4 function in post-mitotic neuron synaptic plasticity