Development of next-gen animal models for fibrous dysplasia (FD)/McCune-Albright syndrome (MAS)

Awardee: J. Silvio Gutkind

Institution: University California San Diego, Moores Cancer Center

Award Amount: $58,500

Funding Period: January 1, 2016 - December 31, 2016

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Dynamic Contrast Enhanced MR Lymphangiogram Imaging of Lymphatic Anomalies (LA)

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Optimizing Delivery and Endpoints of an AAV9-mediated Gene Therapy Trial in AMN