Pharmacologic rescue of telomere defects in dyskeratosis congenita

Awardee: F. Brad Johnson

Institution: University of Pennsylvania

Award Amount: $48,191

Funding Period: January 1, 2018 - December 31, 2018

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Bihormonal Bionic Pancreas for the Treatment of Diabetes Post-Pancreatectomy in Individuals with Congenital Hyperinsulinism – A Pilot Study

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Targeting Endolysosomal Proteins to Treat RASopathies