Functional dissection of CRB1 homophilic interactions in Retinitis pigmentosa

Awardee: Toby Hurd

Institution: University of Edinburgh

Award Amount: $50,497

Funding Period: January 1, 2018 - December 31, 2018

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A New Concept for Gene Delivery and Therapy in Cystic Fib

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CRISPR/Cas9 nuclease design to target allele-specific Collagen VI mutations in patients' fibroblasts