Preclinical Investigations Of Proteasome and Lysosome Inhibitors In CDKL5 Deficient Mice"

Awardee: James Eubanks, PhD

Institution: University Health Network - Krembil Research Institute, Canada

Award Amount: $147,896.00

Funding Period: May 1, 2025 - April 31, 2026

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Exploiting microRNAs to disclose novel pathophysiological mechanisms, biomarkers and therapeutic approaches for CDKL5 deficiency disorder

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An Evaluation of Gene Modification Strategies for Bloom Syndrome