Hematopoietic stem cell gene therapy as a therapeutic approach for CDKL5 Deficiency Disorder

Awardee: Joseph Anderson, PhD

Institution: University of California, Davis

Award Amount: $150,000

Funding Period: May 1, 2022 - April 31, 2023

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A functional genomics approach to dissect the molecular bases of CDKL5 Deficiency Disorder

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Identifying Unmet Care and Communication Needs of Families Affected by Complex Lymphatic Anomalies